Friedreich’s ataxia (FA) is a neurodegenerative disease most people have never heard of, and it remains widely misunderstood —and for the hundreds of Canadians who live with it, the lack of ...

Krystie Maddox, 12, who lives in Wolverhampton with her mother Molvia, 40, a business consultant and stepfather Mitchell, 34, also a consultant, has Friedreich's Ataxia, a rare inherited disorder ...

The firm plans to use improvement in left ventricular mass index and increased frataxin protein expression after LX2006 treatment as co-primary endpoints.