A Prescription Drug User Fee Act (PDUFA) target action date for apitegromab has been set for Sept. 22, 2025.

Since 2016, the FDA has approved three disease-modifying treatments for spinal muscular atrophy, with several ...

The NASA astronaut was stuck in space for over 9 months (286 days appoximately). Although she is back on Earth, her body is ...

Apitegromab is an investigational treatment aimed at improving motor function for people living with spinal muscular atrophy. Scholar Rock said it has also submitted and received validation for its ...

US astronauts Butch Wilmore and Suni Williams are finally coming home — here are some of the health issues they may ...

The Delhi High Court on Monday dismissed an interim injunction application filed by Swiss pharmaceutical giant F Hoffmann-La ...

NASA explains why astronaut Barry "Butch" Wilmore suffered severe muscle loss after 9 months in space, highlighting microgravity's impact and the challenges of recovery.

Video: Spinal Muscular Atrophy: When is Surgical Intervention Appropriate? —How does one time surgery for scoliosis in children with pediatric spinal muscular atrophy get a maximum benefit ...

The challenge of the obesity epidemic is widespread and one that even pediatricians face constantly,” a Connecticut doctor ...