A four-year-old boy with a life-threatening immune disease is now living a normal life thanks to a pioneering gene therapy ...

Despite reports of a sickle cell patient being cured by gene therapy, columnist Oluwatosin Adesoye explains why she remains ...

An investigational gene therapy has successfully restored immune function in all nine children treated with the rare and life ...

The first patient to receive a new gene therapy at the Children's Hospital of Philadelphia is now living pain-free for the ...

An investigational gene therapy has successfully restored immune function in all nine children treated with the rare and life ...

An investigational gene therapy has successfully restored immune function in all nine children treated with the rare and life ...

Korean cell and gene therapy firms seek global growth amid market challenges Korean biotechnology companies explore ...

Hematopoietic stem cells (HSCs) can differentiate into any blood cell. However, as HSCs age, they are more likely to ...

Martin Mwita, 20, is the first patient in St. Louis and among the first across the country to receive a new gene therapy for ...

Gene therapy has emerged as a promising approach to previously untreatable conditions, including Duchenne muscular dystrophy (DMD), a progressive disorder caused by DMD mutations that leads to early ...

Investing in the specialist workforce and overcoming access barriers is essential to successful delivery of this therapy in the NHS, write Jessie Enakhumhe and Yasmin Sheikh Casgevy, or exagamglogene ...