The MOVE-FA trial enrolled 146 pediatric, adolescent and adult patients ... was the change from baseline in the modified Friedreich Ataxia Rating Scale (mFARS) score at week 72.

The follow-up of patients with Friedreich ataxia involves pediatric and adult neurologists, cardiologists, endocrinologists, orthopedists, and allied health professionals such as physical ...

As the only approved treatment to address disease progression, SKYCLARYS addresses a long-standing gap in the care of Canadians living with Friedreich's ataxia Friedreich's ...

"If approved, vatiquinone would be the first therapy for pediatric patients with FA ... stress pathways that are disrupted in Friedreich's ataxia. Inhibition of 15-LO helps to alleviate the ...