People with diseases caused by rare mutations have fewer options and poorer prospects than other patients despite rapid ...

Cystic fibrosis is a disease that it’s caused by a gene mutation, and it causes their mucus to be thicker than a normal person’s. It affects all the systems: your respiratory system ...

The symptoms usually start in early childhood but vary from child to child. Cystic Fibrosis tends to get worse over time as it can be fatal if it leads to a serious infection or the lungs stop ...

lung clearance index (LCI2.5), percent predicted FEV1 (ppFEV1), and the Cystic Fibrosis Questionnaire-Revised (CFQ-R) respiratory domain score. The findings confirm that ELX/TEZ/IVA is generally safe ...

She was diagnosed with cystic fibrosis – an inherited condition that causes mucus ... She continued to see specialists, and they did what they could to help Dedra manage her symptoms, changing ...

It does not necessarily reflect the view of The Herald. A Scottish cystic fibrosis patient who wrote goodbye letters to her family before a revolutionary drug saved her life has turned her ordeal ...

Cystic fibrosis (CF) is an autosomal recessive disease that affects the exocrine glands. These glands, when producing viscous secretions cause manifestations, mainly respiratory and digestive. 1 The ...

FRESNO, Calif. (KFSN) -- Cystic Fibrosis is a genetic disorder that affects the lungs, digestive system and other organs. Babies are screened for it when they are born. Now, those living with the ...

As a cure has not yet been found, standards of care for cystic fibrosis revolve around easing symptoms and improving the quality ... German pharma giant Boehringer Ingelheim along with the UK ...