News

First patient to receive gene therapy treatment developed at Children's Hospital of Philadelphia living pain-free
The first patient to receive a new gene therapy at the Children's Hospital of Philadelphia is now living pain-free for the ...
Investigational gene therapy gives children with rare immune disorder a new lease on life
An investigational gene therapy has successfully restored immune function in all nine children treated with the rare and life ...
Breakthrough gene therapy gives boy with ‘death sentence’ disease a normal life
A boy with an ultra-rare immune disease which can carry a “death sentence” is living a normal life after taking part in a ...
Sickle Cell Disease News1dOpinion
Could gene therapy improve my life as an adult with sickle cell?
Despite reports of a sickle cell patient being cured by gene therapy, columnist Oluwatosin Adesoye explains why she remains ...
Mirage News1d
Gene Therapy Revives Immune Function in Rare Disorder
Key takeawaysTwo years after receiving an investigational gene therapy as part of a clinical trial co-led by UCLA's Dr.
Boy with ‘death sentence’ disease living a normal life after breakthrough gene therapy
A four-year-old boy with a life-threatening immune disease is now living a normal life thanks to a pioneering gene therapy ...
In a first for St. Louis, patient completes new gene therapy to cure sickle cell disease
Martin Mwita, 20, is the first patient in St. Louis and among the first across the country to receive a new gene therapy for ...
London hospital gene therapy breakthrough gives boy with ‘death sentence’ disease a normal life
A boy with an ultra-rare immune disease which can carry a “death sentence” is living a normal life after taking part in a ...
Chosunbiz3d
Korean cell and gene therapy firms seek global growth amid market challenges
Korean cell and gene therapy firms seek global growth amid market challenges Korean biotechnology companies explore ...
Opinion
The BMJ2dOpinion
Casgevy gene therapy could be life changing for people with sickle cell disease
Investing in the specialist workforce and overcoming access barriers is essential to successful delivery of this therapy in the NHS, write Jessie Enakhumhe and Yasmin Sheikh Casgevy, or exagamglogene ...
Laser-based analytical platform enhances CAR T cell therapy manufacturing and effectiveness
A team of researchers from the Keck School of Medicine of USC has developed an advanced tool for analyzing chimeric antigen ...
Fox News1d
Alzheimer’s brain treatment shows promising results in new study
Scientists at the University of California, Irvine, have discovered a "groundbreaking" new therapy to fight the disease. The treatment involves using stem cells to "program" human immune cells ...